Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases

Carlson-Stevermer, J., Das, A., Abdeen, A. A., Fiflis, D., Grindel, B. I., Saxena, S., Akcan, T., Alam, T., Kletzien, H., Kohlenberg, L., Goedland, M., Dombroe, M. J., & Saha, K. (2020). Design of efficacious somatic cell genome editing strategies for recessive and polygenic diseases. Nature Communications, 11(1), 6277. https://doi.org/10.1038/s41467-020-20065-8