Waisman Center
Advancing knowledge of human development, developmental disabilities, and neurodegenerative diseases.

Disease specific therapies in leukodystrophies and leukoencephalopathies

Messing, VMD, PhD, A. Disease Specific Therapies in Leukodystrophies and Leukoencephalopathies.

Helman G, Van Haren K, Bonkowsky JL, Bernard G, Pizzino A, Braverman N, Suhr D, Patterson MC, Ali Fatemi S, Leonard J, van der Knaap MS, Back SA, Damiani S, Goldman SA, Takanohashi A, Petryniak M, Rowitch D, Messing A, Wrabetz L, Schiffmann R, Eichler F. (2015) Disease specific therapies in leukodystrophies and leukoencephalopathies. Molecular Genetics and Metabolism. 114(4):527-36. doi: 10.1016/j.ymgme.2015.01.014.