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Lentiviral mediated RPE65 gene transfer in healthy hiPSCs-derived retinal pigment epithelial cells markedly increased RPE65 mRNA, but modestly protein level

Gamm, MD, PhD, D. Lentiviral Mediated RPE65 Gene Transfer in Healthy HiPSCs-Derived Retinal Pigment Epithelial Cells Markedly Increased RPE65 MRNA, But Modestly Protein Level.
Udry F, Decembrini S, Gamm DM, Déglon N, Kostic C, Arsenijevic Y. (2020). Lentiviral mediated RPE65 gene transfer in healthy hiPSCs-derived retinal pigment epithelial cells markedly increased RPE65 mRNA, but modestly protein level. Science Reports, 10(1):8890. doi: 10.1038/s41598-020-65657-y. PMID: 32483256; PMCID: PMC7264209.