Waisman Center
Advancing knowledge of human development, developmental disabilities, and neurodegenerative diseases.

PMP22 antisense oligonucleotides reverse Charcot-Marie-Tooth disease type 1A features in rodent models

Svaren, PhD, J. PMP22 Antisense Oligonucleotides Reverse Charcot-Marie-Tooth Disease Type 1A Features in Rodent Models.

Zhao HT, Damle S, Ikeda-Lee K, Kuntz S, Li J, Mohan A, Kim A, Hung G, Scheideler MA, Scherer SS, Svaren J, Swayze EE, Kordasiewicz HB. (2018). PMP22 antisense oligonucleotides reverse Charcot-Marie-Tooth disease type 1A features in rodent models. Journal of Clinical Investigation. 128(1):359-368. doi: 10.1172/JCI96499.