Preventing vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA

Akyuz, E., Shahi, P. K., Gissot, L., Saneh, A. A., Sinha, D., Hanstad, G. M., Kabra, M., Zepeda, M. A. F., Gamm, D. M., Young, S. M., Ahern, C. A., & Pattnaik, B. R. (2025). Preventing vision loss in a mouse model of Leber Congenital Amaurosis by engineered tRNA. bioRxiv : the preprint server for biology, 2025.07.10.660754. https://doi.org/10.1101/2025.07.10.660754