Evaluation of subretinally delivered Cas9 ribonucleoproteins in murine and porcine animal models highlights key considerations for therapeutic translation of genetic medicines
Multimodal analyses reveal genes driving electrophysiological maturation of neurons in the primate prefrontal cortex
Genome-Wide CRISPR Screening Identifies Cellular Factors Controlling Nonviral Genome Editing Efficiency
Protocol for comparative gene expression data analysis between brains and organoids using a cloud-based web app
AAV vector-derived elements integrate into Cas9-generated double-strand breaks and disrupt gene transcription.
Heterogeneity in the progression of retinal pathologies in mice harboring patient mimicking Impg2 mutations