Human spinal GABA neurons alleviate spasticity and improve locomotion in rats with spinal cord injury
Impaired lipid metabolism in astrocytes underlies degeneration of cortical projection neurons in hereditary spastic paraplegia
Human iPSC Modeling Reveals Mutation-Specific Responses to Gene Therapy in a Genotypically Diverse Dominant Maculopathy
Advances in Human Stem Cells and Genome Editing to Understand and Develop Treatment for Fragile X Syndrome
Lentiviral mediated RPE65 gene transfer in healthy hiPSCs-derived retinal pigment epithelial cells markedly increased RPE65 mRNA, but modestly protein level
